Clinical trials
Hemoglobinopathies trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
58 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 2 |
| 2001 | 2 |
| 2002 | 1 |
| 2004 | 1 |
| 2005 | 3 |
| 2006 | 1 |
| 2008 | 2 |
| 2009 | 3 |
| 2011 | 1 |
| 2012 | 1 |
| 2013 | 3 |
| 2014 | 2 |
| 2015 | 2 |
| 2016 | 1 |
| 2017 | 5 |
| 2018 | 2 |
| 2019 | 1 |
| 2020 | 3 |
| 2021 | 3 |
| 2022 | 8 |
| 2023 | 1 |
| 2024 | 3 |
| 2025 | 3 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 20 |
| Recruiting | 14 |
| Terminated | 10 |
| Active, not recruiting | 8 |
| Unknown status | 2 |
| Enrolling by invitation | 2 |
| No longer available | 1 |
| Not yet recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Vertex Pharmaceuticals Incorporated | 6 |
| University of California, San Francisco | 5 |
| Baylor College of Medicine | 4 |
| Editas Medicine, Inc. | 3 |
| Children's Hospital of Philadelphia | 2 |
| Diane George | 2 |
| Forma Therapeutics, Inc. | 2 |
| Fred Hutchinson Cancer Center | 2 |
| Masonic Cancer Center, University of Minnesota | 2 |
| National Institute of Allergy and Infectious Diseases (NIAID) | 2 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Hemoglobinopathies | 58 |
| Anemia, Sickle Cell | 35 |
| Thalassemia | 22 |
| Hematologic Diseases | 14 |
| Bone Marrow Failure Disorders | 12 |
| Immunologic Deficiency Syndromes | 11 |
| beta-Thalassemia | 11 |
| Genetic Diseases, Inborn | 10 |
| Anemia | 7 |
| Anemia, Aplastic | 6 |
Trials
Showing 1 to 25 of 58. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.