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Clinical trials

Observational Hemoglobinopathies trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Hemoglobinopathies Phase: Observational Country / region: United States Clear all

13 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20051
20061
20111
20151
20161
20171
20201
20222
20241
20252
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed6
Recruiting5
Enrolling by invitation1
Terminated1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
University of California, San Francisco4
St. Jude Children's Research Hospital2
Beam Therapeutics Inc.1
Columbia University1
Cyprus Institute of Neurology and Genetics1
Editas Medicine, Inc.1
Medical College of Wisconsin1
National Institute of Allergy and Infectious Diseases (NIAID)1
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Hemoglobinopathies13
Anemia, Sickle Cell7
Thalassemia6
Fanconi Anemia4
Hematologic Neoplasms4
Immunologic Deficiency Syndromes4
Anemia2
beta-Thalassemia2
Anemia, Aplastic1
Anemia, Hemolytic1

Trials

Showing 1 to 13 of 13. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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