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Clinical trials

Completed Hemoglobinopathies trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Hemoglobinopathies Status: Completed Country / region: United States Clear all

20 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20021
20041
20052
20061
20082
20091
20111
20151
20161
20173
20182
20201
20222

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed20

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
University of California, San Francisco4
Vertex Pharmaceuticals Incorporated2
Ann & Robert H Lurie Children's Hospital of Chicago1
Baylor College of Medicine1
Children's Hospital of Philadelphia1
Columbia University1
Dana-Farber Cancer Institute1
Duke University1
Forma Therapeutics, Inc.1
Fred Hutchinson Cancer Center1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Hemoglobinopathies20
Anemia, Sickle Cell13
Thalassemia11
Immunologic Deficiency Syndromes7
Hematologic Diseases5
Fanconi Anemia4
Hematologic Neoplasms4
Genetic Diseases, Inborn3
beta-Thalassemia3
Anemia2

Trials

Showing 1 to 20 of 20. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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