Clinical trials
Hemoglobinuria, Paroxysmal trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
68 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 3 |
| 2002 | 3 |
| 2003 | 1 |
| 2004 | 4 |
| 2005 | 4 |
| 2006 | 3 |
| 2007 | 1 |
| 2008 | 1 |
| 2009 | 4 |
| 2010 | 1 |
| 2011 | 2 |
| 2012 | 2 |
| 2014 | 1 |
| 2015 | 1 |
| 2016 | 1 |
| 2017 | 6 |
| 2018 | 4 |
| 2019 | 3 |
| 2020 | 2 |
| 2021 | 5 |
| 2022 | 4 |
| 2023 | 1 |
| 2024 | 4 |
| 2025 | 3 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 44 |
| Recruiting | 9 |
| Active, not recruiting | 7 |
| Terminated | 5 |
| Enrolling by invitation | 1 |
| Approved for marketing | 1 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Alexion Pharmaceuticals, Inc. | 18 |
| National Heart, Lung, and Blood Institute (NHLBI) | 6 |
| Novartis Pharmaceuticals | 5 |
| St. Jude Children's Research Hospital | 5 |
| Apellis Pharmaceuticals, Inc. | 3 |
| Roswell Park Cancer Institute | 3 |
| Fred Hutchinson Cancer Center | 2 |
| Masonic Cancer Center, University of Minnesota | 2 |
| Regeneron Pharmaceuticals | 2 |
| Scripps Health | 2 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Hemoglobinuria, Paroxysmal | 68 |
| Anemia, Aplastic | 15 |
| Myelodysplastic Syndromes | 14 |
| Leukemia, Myeloid, Acute | 12 |
| Lymphoma, Non-Hodgkin | 12 |
| Precursor Cell Lymphoblastic Leukemia-Lymphoma | 10 |
| Hodgkin Disease | 9 |
| Multiple Myeloma | 8 |
| Leukemia, Myelogenous, Chronic, BCR-ABL Positive | 7 |
| Leukemia, Myelomonocytic, Juvenile | 7 |
Trials
Showing 1 to 25 of 68. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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