Clinical trials
Phase 3 Hemoglobinuria, Paroxysmal trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
22 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2002 | 2 |
| 2004 | 3 |
| 2005 | 2 |
| 2016 | 1 |
| 2017 | 1 |
| 2018 | 2 |
| 2019 | 2 |
| 2020 | 2 |
| 2021 | 2 |
| 2022 | 3 |
| 2023 | 1 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 16 |
| Active, not recruiting | 4 |
| Recruiting | 1 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Alexion Pharmaceuticals, Inc. | 9 |
| Novartis Pharmaceuticals | 4 |
| National Heart, Lung, and Blood Institute (NHLBI) | 2 |
| Regeneron Pharmaceuticals | 2 |
| St. Jude Children's Research Hospital | 2 |
| Amgen | 1 |
| Apellis Pharmaceuticals, Inc. | 1 |
| Hoffmann-La Roche | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Hemoglobinuria, Paroxysmal | 22 |
| Anemia | 3 |
| Hemolysis | 3 |
| Leukemia, Myeloid, Acute | 2 |
| Leukemia, Myelomonocytic, Juvenile | 2 |
| Lymphoma, Non-Hodgkin | 2 |
| Myelodysplastic Syndromes | 2 |
| Hemoglobinuria | 1 |
| Leukemia | 1 |
| Leukemia, Myelogenous, Chronic, BCR-ABL Positive | 1 |
Trials
Showing 1 to 22 of 22. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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