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Clinical trials

Completed Phase 2 Infant, Newborn, Diseases trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Infant, Newborn, Diseases Phase: Phase 2 Status: Completed Clear all

10 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20072
20091
20101
20121
20141

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed10

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Kastle Therapeutics, LLC2
National Center for Research Resources (NCRR)2
Vertex Pharmaceuticals Incorporated2
Alexion Pharmaceuticals, Inc.1
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)1
Johns Hopkins Bloomberg School of Public Health1
Universitaire Ziekenhuizen KU Leuven1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Infant, Newborn, Diseases10
Genetic Diseases, Inborn5
Lipid Metabolism Disorders3
Lipid Metabolism, Inborn Errors3
Metabolic Diseases3
Metabolism, Inborn Errors3
Congenital Abnormalities2
Cystic Fibrosis2
Dyslipidemias2
Hypercholesterolemia2

Trials

Showing 1 to 10 of 10. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

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