Clinical trials
Observational Mucopolysaccharidosis I trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
17 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 1 |
| 2007 | 1 |
| 2009 | 2 |
| 2010 | 1 |
| 2011 | 1 |
| 2012 | 1 |
| 2014 | 1 |
| 2018 | 2 |
| 2019 | 1 |
| 2020 | 2 |
| 2022 | 2 |
| 2023 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 6 |
| Terminated | 5 |
| Active, not recruiting | 2 |
| Recruiting | 2 |
| Enrolling by invitation | 1 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| University of Minnesota | 3 |
| Masonic Cancer Center, University of Minnesota | 2 |
| Fairview University Medical Center | 1 |
| Genzyme, a Sanofi Company | 1 |
| Magenta Therapeutics, Inc. | 1 |
| National MPS Society | 1 |
| Paul Szabolcs | 1 |
| REGENXBIO Inc. | 1 |
| RTI International | 1 |
| Sangamo Therapeutics | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis I | 17 |
| Mucopolysaccharidosis II | 7 |
| Mucopolysaccharidosis VI | 7 |
| Mucopolysaccharidoses | 6 |
| Leukodystrophy, Globoid Cell | 5 |
| Leukodystrophy, Metachromatic | 4 |
| Mucopolysaccharidosis IV | 4 |
| Sudden Infant Death | 4 |
| Gaucher Disease | 3 |
| Mucopolysaccharidosis III | 3 |
Trials
Showing 1 to 17 of 17. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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