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Clinical trials

Completed Observational Mucopolysaccharidosis I trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Mucopolysaccharidosis I Phase: Observational Status: Completed Clear all

9 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20031
20071
20092
20101
20171
20181
20211
20221

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed9

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
University of Minnesota3
Centre Hospitalier Universitaire de Liege1
Genzyme, a Sanofi Company1
Sanofi1
St. Jude Children's Research Hospital1
University Hospital Heidelberg1
University of Chicago1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Mucopolysaccharidosis I9
Mucopolysaccharidosis II4
Mucopolysaccharidosis III3
Mucopolysaccharidosis VI3
Glycogen Storage Disease Type II2
Mucopolysaccharidoses2
Mucopolysaccharidosis IV2
Mucopolysaccharidosis VII2
Severe Combined Immunodeficiency2
Sudden Infant Death2

Trials

Showing 1 to 9 of 9. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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