Clinical trials
Phase 1 Mucopolysaccharidosis I trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
12 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2005 | 2 |
| 2008 | 3 |
| 2012 | 1 |
| 2013 | 1 |
| 2014 | 1 |
| 2015 | 2 |
| 2023 | 1 |
| 2024 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 8 |
| Recruiting | 2 |
| Terminated | 2 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| ArmaGen, Inc | 2 |
| Masonic Cancer Center, University of Minnesota | 2 |
| Patricia I. Dickson, M.D. | 2 |
| Duke University | 1 |
| Emory University | 1 |
| Immusoft of CA, Inc. | 1 |
| Joanne Kurtzberg, MD | 1 |
| New York Medical College | 1 |
| West China Hospital | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis I | 12 |
| Anemia, Aplastic | 3 |
| Anemia, Diamond-Blackfan | 3 |
| Lysosomal Storage Diseases | 3 |
| Metabolism, Inborn Errors | 3 |
| Mucopolysaccharidoses | 2 |
| Mucopolysaccharidosis II | 2 |
| Spinal Cord Compression | 2 |
| Adrenoleukodystrophy | 1 |
| Anemia, Sickle Cell | 1 |
Trials
Showing 1 to 12 of 12. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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