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Clinical trials

Completed Phase 1 Mucopolysaccharidosis I trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Mucopolysaccharidosis I Phase: Phase 1 Status: Completed Clear all

8 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20051
20082
20121
20131
20141
20152

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed8

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
ArmaGen, Inc2
Masonic Cancer Center, University of Minnesota2
Duke University1
Emory University1
Joanne Kurtzberg, MD1
New York Medical College1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Mucopolysaccharidosis I8
Anemia, Aplastic3
Anemia, Diamond-Blackfan3
Metabolism, Inborn Errors3
Mucopolysaccharidosis II2
Adrenoleukodystrophy1
Anemia, Sickle Cell1
Chediak-Higashi Syndrome1
Dyskeratosis Congenita1
Fanconi Anemia1

Trials

Showing 1 to 8 of 8. Each trial links to its page on Pharma Observatory.

Recently changed trials

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