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Clinical trials

Terminated Phase 1 Metabolic Diseases trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Metabolic Diseases Phase: Phase 1 Status: Terminated Clear all

5 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20111
20152
20161
20231

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Terminated5

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Bellicum Pharmaceuticals1
CRISPR Therapeutics AG1
Dicerna Pharmaceuticals, Inc., a Novo Nordisk company1
Fate Therapeutics1
Ira Fox1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Metabolic Diseases5
Anemia, Diamond-Blackfan1
Anemia, Sickle Cell1
Autoimmune Diseases1
Carbamoyl-Phosphate Synthase I Deficiency Disease1
Citrullinemia1
Congenital Bone Marrow Failure Syndromes1
Crigler-Najjar Syndrome1
Diabetes Mellitus1
Diabetes Mellitus, Type 11

Trials

Showing 1 to 5 of 5. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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