Clinical trials
Metabolism, Inborn Errors trials in the United Kingdom
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
23 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2007 | 1 |
| 2008 | 1 |
| 2013 | 1 |
| 2014 | 1 |
| 2015 | 1 |
| 2017 | 2 |
| 2018 | 4 |
| 2019 | 1 |
| 2021 | 4 |
| 2022 | 1 |
| 2023 | 1 |
| 2024 | 2 |
| 2026 | 3 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 13 |
| Recruiting | 5 |
| Active, not recruiting | 2 |
| Terminated | 2 |
| Not yet recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| ModernaTX, Inc. | 5 |
| Alexion Pharmaceuticals, Inc. | 3 |
| Dr. Schär AG / SPA | 2 |
| Kastle Therapeutics, LLC | 2 |
| Vitaflo International, Ltd | 2 |
| iECURE, Inc. | 2 |
| Alnylam Pharmaceuticals | 1 |
| HemoShear Therapeutics | 1 |
| JCR Pharmaceuticals Co., Ltd. | 1 |
| Manchester University NHS Foundation Trust | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Metabolism, Inborn Errors | 23 |
| Genetic Diseases, Inborn | 15 |
| Metabolic Diseases | 14 |
| Amino Acid Metabolism, Inborn Errors | 5 |
| Phenylketonurias | 5 |
| Brain Diseases, Metabolic, Inborn | 4 |
| Propionic Acidemia | 4 |
| Brain Diseases | 3 |
| Brain Diseases, Metabolic | 3 |
| Central Nervous System Diseases | 3 |
Trials
Showing 1 to 23 of 23. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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