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Clinical trials

Terminated Metabolism, Inborn Errors trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Metabolism, Inborn Errors Status: Terminated Country / region: United States Clear all

11 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20082
20151
20215
20221
20231

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Terminated11

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
HemoShear Therapeutics2
SwanBio Therapeutics, Inc.2
Aldagen1
Hugo W. Moser Research Institute at Kennedy Krieger, Inc.1
LogicBio Therapeutics, Inc1
Masonic Cancer Center, University of Minnesota1
ModernaTX, Inc.1
Shire1
Synlogic1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Metabolism, Inborn Errors11
Metabolic Diseases5
Adrenoleukodystrophy4
Genetic Diseases, Inborn4
Brain Diseases, Metabolic, Inborn3
Demyelinating Diseases3
Hereditary Central Nervous System Demyelinating Diseases3
Leukodystrophy, Metachromatic3
Peroxisomal Disorders3
Sphingolipidoses3

Trials

Showing 1 to 11 of 11. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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