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Clinical trials

Terminated Observational Metabolism, Inborn Errors trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Metabolism, Inborn Errors Phase: Observational Status: Terminated Clear all

4 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20151
20212

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Terminated4

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Assistance Publique - Hôpitaux de Paris1
HemoShear Therapeutics1
Shire1
SwanBio Therapeutics, Inc.1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Metabolism, Inborn Errors4
Metabolic Diseases3
Brain Diseases, Metabolic, Inborn2
Demyelinating Diseases2
Genetic Diseases, Inborn2
Hereditary Central Nervous System Demyelinating Diseases2
Adrenal Insufficiency1
Adrenoleukodystrophy1
Brain Diseases1
Brain Diseases, Metabolic1

Trials

Showing 1 to 4 of 4. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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