Clinical trials
Completed Phase 1 Metabolism, Inborn Errors trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
9 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2005 | 1 |
| 2008 | 1 |
| 2013 | 1 |
| 2022 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 9 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Center for Research Resources (NCRR) | 4 |
| Duke University | 1 |
| Joanne Kurtzberg, MD | 1 |
| National Institute of Mental Health (NIMH) | 1 |
| New York Medical College | 1 |
| Synlogic | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Metabolism, Inborn Errors | 9 |
| Rare Diseases | 4 |
| Gaucher Disease | 3 |
| Mucopolysaccharidosis I | 3 |
| Anemia, Aplastic | 2 |
| Anemia, Diamond-Blackfan | 2 |
| Mucopolysaccharidosis II | 2 |
| Porphyrias | 2 |
| Adrenoleukodystrophy | 1 |
| Fucosidosis | 1 |
Trials
Showing 1 to 9 of 9. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.