Clinical trials
Withdrawn Phase 1 Metabolism, Inborn Errors trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
2 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2009 | 1 |
| 2015 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Withdrawn | 2 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Joanne Kurtzberg, MD | 1 |
| Neurocrine Biosciences | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Metabolism, Inborn Errors | 2 |
| Adrenal Gland Diseases | 1 |
| Adrenal Hyperplasia, Congenital | 1 |
| Adrenocortical Hyperfunction | 1 |
| Adrenogenital Syndrome | 1 |
| Congenital Abnormalities | 1 |
| Disorders of Sex Development | 1 |
| Endocrine System Diseases | 1 |
| Gangliosidoses, GM2 | 1 |
| Genetic Diseases, Inborn | 1 |
Trials
Showing 1 to 2 of 2. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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