Clinical trials
Phase 3 Metabolism, Inborn Errors trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
15 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2004 | 1 |
| 2007 | 1 |
| 2008 | 2 |
| 2009 | 4 |
| 2023 | 1 |
| 2024 | 2 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 10 |
| Recruiting | 2 |
| Terminated | 2 |
| Active, not recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Regeneron Pharmaceuticals | 4 |
| Kastle Therapeutics, LLC | 2 |
| Aldagen | 1 |
| Arrowhead Pharmaceuticals | 1 |
| Brigham and Women's Hospital | 1 |
| Intellia Therapeutics | 1 |
| National Center for Research Resources (NCRR) | 1 |
| National Heart, Lung, and Blood Institute (NHLBI) | 1 |
| Synlogic | 1 |
| University of Florida | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Metabolism, Inborn Errors | 15 |
| Genetic Diseases, Inborn | 9 |
| Metabolic Diseases | 9 |
| Arthritis | 4 |
| Gout | 4 |
| Joint Diseases | 4 |
| Musculoskeletal Diseases | 4 |
| Purine-Pyrimidine Metabolism, Inborn Errors | 4 |
| Rheumatic Diseases | 4 |
| Dyslipidemias | 3 |
Trials
Showing 1 to 15 of 15. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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