Clinical trials
Completed Metabolism, Inborn Errors trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
87 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 3 |
| 2004 | 2 |
| 2005 | 2 |
| 2006 | 5 |
| 2007 | 2 |
| 2008 | 2 |
| 2009 | 5 |
| 2011 | 2 |
| 2012 | 1 |
| 2013 | 3 |
| 2014 | 3 |
| 2015 | 2 |
| 2016 | 1 |
| 2017 | 4 |
| 2018 | 6 |
| 2019 | 6 |
| 2020 | 1 |
| 2021 | 3 |
| 2022 | 2 |
| 2023 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 87 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Center for Research Resources (NCRR) | 23 |
| Kastle Therapeutics, LLC | 4 |
| Regeneron Pharmaceuticals | 4 |
| Alexion Pharmaceuticals, Inc. | 3 |
| University of Lausanne | 3 |
| Alnylam Pharmaceuticals | 2 |
| Dr. Schär AG / SPA | 2 |
| Duke University | 2 |
| FDA Office of Orphan Products Development | 2 |
| Fred Hutchinson Cancer Center | 2 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Metabolism, Inborn Errors | 87 |
| Rare Diseases | 31 |
| Genetic Diseases, Inborn | 24 |
| Metabolic Diseases | 20 |
| Porphyrias | 9 |
| Lipid Metabolism Disorders | 7 |
| Lipid Metabolism, Inborn Errors | 7 |
| Lysosomal Storage Diseases | 7 |
| Phenylketonurias | 7 |
| Infant, Newborn, Diseases | 6 |
Trials
Showing 1 to 25 of 87. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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