Clinical trials
Completed Observational Mucopolysaccharidosis III trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
12 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2009 | 1 |
| 2010 | 2 |
| 2012 | 2 |
| 2013 | 2 |
| 2014 | 1 |
| 2015 | 1 |
| 2017 | 1 |
| 2022 | 1 |
| 2023 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 12 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Alexion Pharmaceuticals, Inc. | 2 |
| Shire | 2 |
| University of Minnesota | 2 |
| Allievex Corporation | 1 |
| Nationwide Children's Hospital | 1 |
| Phoenix Nest | 1 |
| Sanguine Biosciences | 1 |
| University Hospital Heidelberg | 1 |
| University of Chicago | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis III | 12 |
| Mucopolysaccharidoses | 5 |
| Mucopolysaccharidosis I | 3 |
| Mucopolysaccharidosis II | 2 |
| Mucopolysaccharidosis VI | 2 |
| Sudden Infant Death | 2 |
| Cognitive Dysfunction | 1 |
| Genetic Diseases, Inborn | 1 |
| Leukodystrophy, Globoid Cell | 1 |
| Mental Disorders | 1 |
Trials
Showing 1 to 12 of 12. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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