Clinical trials
Terminated Phase 1/2 Mucopolysaccharidosis III trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
5 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2011 | 2 |
| 2015 | 1 |
| 2017 | 1 |
| 2019 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Terminated | 5 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Abeona Therapeutics, Inc | 1 |
| Alexion Pharmaceuticals, Inc. | 1 |
| Shire | 1 |
| Talaris Therapeutics Inc. | 1 |
| Ultragenyx Pharmaceutical Inc | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis III | 5 |
| Adrenoleukodystrophy | 1 |
| Leukodystrophy, Globoid Cell | 1 |
| Leukodystrophy, Metachromatic | 1 |
| Lysosomal Storage Diseases | 1 |
| Mucopolysaccharidosis I | 1 |
| Mucopolysaccharidosis II | 1 |
| Niemann-Pick Diseases | 1 |
| Sandhoff Disease | 1 |
| Sudden Infant Death | 1 |
Trials
Showing 1 to 5 of 5. Each trial links to its page on Pharma Observatory.
Recently changed trials
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