Clinical trials
Completed Observational Mucopolysaccharidosis IV trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
18 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2009 | 1 |
| 2012 | 2 |
| 2013 | 3 |
| 2014 | 2 |
| 2017 | 1 |
| 2018 | 2 |
| 2019 | 2 |
| 2022 | 1 |
| 2023 | 1 |
| 2024 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 18 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Nadia Ali, PhD | 2 |
| BioMarin Pharmaceutical | 1 |
| CENTOGENE GmbH Rostock | 1 |
| Centre Hospitalier Universitaire de Liege | 1 |
| Children's Hospital of Eastern Ontario | 1 |
| Children's Hospitals and Clinics of Minnesota | 1 |
| Ciusss de L'Est de l'Île de Montréal | 1 |
| Emory University | 1 |
| GOIZET | 1 |
| Greenwood Genetic Center | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis IV | 18 |
| Mucopolysaccharidosis VI | 4 |
| Dwarfism | 2 |
| Genetic Diseases, Inborn | 2 |
| Mucopolysaccharidoses | 2 |
| Mucopolysaccharidosis I | 2 |
| Mucopolysaccharidosis II | 2 |
| Mucopolysaccharidosis VII | 2 |
| Osteochondrodysplasias | 2 |
| Respiratory Aspiration | 2 |
Trials
Showing 1 to 18 of 18. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.