Clinical trials
Recruiting Observational Mucopolysaccharidosis IV trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
12 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2012 | 1 |
| 2015 | 1 |
| 2017 | 1 |
| 2020 | 1 |
| 2021 | 1 |
| 2022 | 3 |
| 2024 | 1 |
| 2025 | 3 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 12 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | 2 |
| Children's Hospital of Orange County | 1 |
| Innoskel | 1 |
| Institut National de la Santé Et de la Recherche Médicale, France | 1 |
| Karolinska Institutet | 1 |
| Luca Sangiorgi | 1 |
| Nemours Children's Clinic | 1 |
| QED Therapeutics, a BridgeBio company | 1 |
| University Hospital, Angers | 1 |
| University of California, San Francisco | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis IV | 12 |
| Dwarfism | 4 |
| Bone Diseases | 2 |
| Gaucher Disease | 2 |
| Lysosomal Storage Diseases | 2 |
| Mucopolysaccharidoses | 2 |
| Mucopolysaccharidosis I | 2 |
| Mucopolysaccharidosis II | 2 |
| Mucopolysaccharidosis III | 2 |
| Mucopolysaccharidosis VI | 2 |
Trials
Showing 1 to 12 of 12. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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