Clinical trials
Completed Mucopolysaccharidosis IV trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
50 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2006 | 1 |
| 2008 | 1 |
| 2009 | 3 |
| 2010 | 2 |
| 2011 | 3 |
| 2012 | 3 |
| 2013 | 6 |
| 2014 | 4 |
| 2016 | 2 |
| 2017 | 1 |
| 2018 | 3 |
| 2019 | 5 |
| 2020 | 2 |
| 2021 | 1 |
| 2022 | 2 |
| 2023 | 4 |
| 2024 | 2 |
| 2025 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 50 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| BioMarin Pharmaceutical | 6 |
| QED Therapeutics, a BridgeBio company | 3 |
| Nadia Ali, PhD | 2 |
| State Key Laboratory of Respiratory Disease | 2 |
| Supplement Formulators, Inc. | 2 |
| The Canadian College of Naturopathic Medicine | 2 |
| Acuity Polymers, Inc. | 1 |
| Ain Shams University | 1 |
| BIO-CAT Microbials, LLC | 1 |
| CENTOGENE GmbH Rostock | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis IV | 50 |
| Diarrhea | 8 |
| Constipation | 7 |
| Respiratory Aspiration | 6 |
| Abdominal Pain | 5 |
| Genetic Diseases, Inborn | 5 |
| Dwarfism | 4 |
| Irritable Bowel Syndrome | 4 |
| Lysosomal Storage Diseases | 4 |
| Mucopolysaccharidosis VI | 4 |
Trials
Showing 1 to 25 of 50. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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