Clinical trials
Recruiting Mucopolysaccharidosis IV trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
18 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2012 | 1 |
| 2015 | 1 |
| 2017 | 1 |
| 2019 | 1 |
| 2020 | 1 |
| 2021 | 2 |
| 2022 | 3 |
| 2024 | 2 |
| 2025 | 4 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 18 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | 2 |
| QED Therapeutics, a BridgeBio company | 2 |
| University of California, San Francisco | 2 |
| Children's Hospital of Orange County | 1 |
| Hospital for Special Surgery, New York | 1 |
| Innoskel | 1 |
| Institut National de la Santé Et de la Recherche Médicale, France | 1 |
| Karolinska Institutet | 1 |
| Kiwi Health Inc | 1 |
| Luca Sangiorgi | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis IV | 18 |
| Dwarfism | 5 |
| Bone Diseases | 3 |
| Gaucher Disease | 3 |
| Mucopolysaccharidosis VI | 3 |
| Mucopolysaccharidosis VII | 3 |
| Irritable Bowel Syndrome | 2 |
| Lysosomal Storage Diseases | 2 |
| Mucopolysaccharidoses | 2 |
| Mucopolysaccharidosis I | 2 |
Trials
Showing 1 to 18 of 18. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.