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Clinical trials

Phase 1/2 Muscular Diseases trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Diseases Phase: Phase 1/2 Country / region: United States Clear all

6 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20121
20151
20161
20221
20241

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed3
Active, not recruiting1
Not yet recruiting1
Recruiting1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Craig McDonald, MD1
George Washington University1
National Human Genome Research Institute (NHGRI)1
National Institute of Nursing Research (NINR)1
Texas Tech University Health Sciences Center1
Vertex Pharmaceuticals Incorporated1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Diseases6
Mitochondrial Diseases2
Neuromuscular Diseases2
Acidosis, Lactic1
Anxiety Disorders1
Cardiomyopathies1
Cognition Disorders1
Dystonia1
Genetic Diseases, Inborn1
Hearing Loss1

Trials

Showing 1 to 6 of 6. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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