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Clinical trials

Phase 1 Muscular Dystrophies trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophies Phase: Phase 1 Country / region: United States Clear all

15 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20081
20091
20101
20111
20121
20141
20151
20171
20181
20222
20232
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed13
Recruiting1
Terminated1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Nationwide Children's Hospital3
Cedars-Sinai Medical Center2
Edgewise Therapeutics, Inc.2
GlaxoSmithKline2
Allergy and Asthma Consultants, Wichita, Kansas1
Cure Rare Disease, Inc1
Jerry R. Mendell1
PepGen Inc1
University of North Carolina, Chapel Hill1
Vanderbilt University Medical Center1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophies15
Muscular Dystrophy, Duchenne10
Genetic Diseases, Inborn2
Muscular Diseases2
Muscular Disorders, Atrophic2
Musculoskeletal Diseases2
Nervous System Diseases2
Neuromuscular Diseases2
Cardiomyopathies1
Heart Failure1

Trials

Showing 1 to 15 of 15. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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