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Clinical trials

Completed Phase 1 Muscular Dystrophies trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophies Phase: Phase 1 Status: Completed Clear all

14 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20081
20091
20101
20112
20121
20141
20151
20181
20222
20232

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed14

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Nationwide Children's Hospital3
Edgewise Therapeutics, Inc.2
GlaxoSmithKline2
Allergy and Asthma Consultants, Wichita, Kansas1
Cedars-Sinai Medical Center1
Cure Rare Disease, Inc1
Jerry R. Mendell1
Parent Project, Italy1
PepGen Inc1
University of North Carolina, Chapel Hill1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophies14
Muscular Dystrophy, Duchenne9
Genetic Diseases, Inborn2
Muscular Diseases2
Muscular Disorders, Atrophic2
Musculoskeletal Diseases2
Nervous System Diseases2
Neuromuscular Diseases2
Heredodegenerative Disorders, Nervous System1
Muscular Dystrophies, Limb-Girdle1

Trials

Showing 1 to 14 of 14. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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