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Clinical trials

Phase 2 Myotonic Dystrophy trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Myotonic Dystrophy Phase: Phase 2 Country / region: United States Clear all

5 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20071
20111
20211
20221
20251

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed4
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Avidity Biosciences, Inc.1
Harmony Biosciences Management, Inc.1
Insmed Incorporated1
University of Rochester1
Vertex Pharmaceuticals Incorporated1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Myotonic Dystrophy5
Muscular Dystrophies3
Genetic Diseases, Inborn2
Heredodegenerative Disorders, Nervous System2
Muscular Diseases2
Muscular Disorders, Atrophic2
Musculoskeletal Diseases2
Myotonic Disorders2
Nervous System Diseases2
Neurodegenerative Diseases2

Trials

Showing 1 to 5 of 5. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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