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Clinical trials

Phase 2 Myotonic Dystrophy trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Myotonic Dystrophy Phase: Phase 2 Clear all

8 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20071
20111
20161
20211
20221
20241
20252

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed5
Recruiting2
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
PepGen Inc2
AMO Pharma Limited1
Avidity Biosciences, Inc.1
Harmony Biosciences Management, Inc.1
Insmed Incorporated1
University of Rochester1
Vertex Pharmaceuticals Incorporated1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Myotonic Dystrophy8
Genetic Diseases, Inborn3
Heredodegenerative Disorders, Nervous System3
Muscular Diseases3
Muscular Disorders, Atrophic3
Muscular Dystrophies3
Musculoskeletal Diseases3
Myotonic Disorders3
Nervous System Diseases3
Neuromuscular Diseases3

Trials

Showing 1 to 8 of 8. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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