Clinical trials
Enrolling by invitation Myotonic Dystrophy trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
10 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2008 | 1 |
| 2013 | 1 |
| 2021 | 1 |
| 2023 | 1 |
| 2024 | 2 |
| 2025 | 4 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Enrolling by invitation | 10 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| LMU Klinikum | 2 |
| Avidity Biosciences, Inc. | 1 |
| First Affiliated Hospital of Fujian Medical University | 1 |
| Huashan Hospital | 1 |
| Johns Hopkins University | 1 |
| Lupin Ltd. | 1 |
| Sarepta Therapeutics, Inc. | 1 |
| Vertex Pharmaceuticals Incorporated | 1 |
| Wake Forest University Health Sciences | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Myotonic Dystrophy | 10 |
| Muscular Dystrophies | 3 |
| Neuromuscular Diseases | 3 |
| Friedreich Ataxia | 2 |
| Glycogen Storage Disease Type II | 2 |
| Guillain-Barre Syndrome | 2 |
| Hereditary Sensory and Motor Neuropathy | 2 |
| Lambert-Eaton Myasthenic Syndrome | 2 |
| Muscular Atrophy, Spinal | 2 |
| Muscular Dystrophy, Facioscapulohumeral | 2 |
Trials
Showing 1 to 10 of 10. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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