Clinical trials
Congenital, Hereditary, and Neonatal Diseases and Abnormalities trials in the United Kingdom
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
10 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2011 | 1 |
| 2017 | 3 |
| 2018 | 2 |
| 2022 | 2 |
| 2025 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 5 |
| Recruiting | 4 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Children's Hospital of Philadelphia | 1 |
| Fresenius Medical Care Deutschland GmbH | 1 |
| Golden Jubilee National Hospital | 1 |
| JCR Pharmaceuticals Co., Ltd. | 1 |
| King's College Hospital NHS Trust | 1 |
| The Royal Wolverhampton Hospitals NHS Trust | 1 |
| The Wellcome Sanger Institute | 1 |
| University College London Hospitals | 1 |
| University Hospital, Gasthuisberg | 1 |
| Xim Limited | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Congenital, Hereditary, and Neonatal Diseases and Abnormalities | 10 |
| Brain Diseases, Metabolic, Inborn | 1 |
| Carbohydrate Metabolism, Inborn Errors | 1 |
| Cardiovascular Diseases | 1 |
| Fucosidosis | 1 |
| Genetic Diseases, Inborn | 1 |
| Heart Diseases | 1 |
| Hernia, Diaphragmatic | 1 |
| Lysosomal Storage Diseases | 1 |
| Lysosomal Storage Diseases, Nervous System | 1 |
Trials
Showing 1 to 10 of 10. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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