Clinical trials
Observational Congenital, Hereditary, and Neonatal Diseases and Abnormalities trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
61 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 2 |
| 2001 | 5 |
| 2002 | 7 |
| 2003 | 1 |
| 2004 | 6 |
| 2005 | 5 |
| 2006 | 5 |
| 2007 | 3 |
| 2008 | 1 |
| 2010 | 1 |
| 2016 | 1 |
| 2022 | 1 |
| 2025 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Terminated | 37 |
| Completed | 18 |
| Recruiting | 3 |
| Withdrawn | 2 |
| Active, not recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Children's Healthcare of Atlanta | 47 |
| Emory University | 9 |
| Children's Hospital of Philadelphia | 1 |
| JCR Pharmaceuticals Co., Ltd. | 1 |
| National Human Genome Research Institute (NHGRI) | 1 |
| Prime Medicine, Inc. | 1 |
| University of Arizona | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Congenital, Hereditary, and Neonatal Diseases and Abnormalities | 61 |
| Heart Defects, Congenital | 8 |
| Genetic Diseases, Inborn | 3 |
| Congenital Abnormalities | 2 |
| Cyanosis | 2 |
| Down Syndrome | 2 |
| Heart Failure | 2 |
| Metabolism, Inborn Errors | 2 |
| Univentricular Heart | 2 |
| Aneurysm | 1 |
Trials
Showing 1 to 25 of 61. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.