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Clinical trials

Phase 3 Neuromuscular Diseases trials in the United Kingdom

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Neuromuscular Diseases Phase: Phase 3 Country / region: United Kingdom Clear all

12 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20132
20141
20151
20181
20191
20211
20223
20231
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed5
Terminated4
Active, not recruiting2
Recruiting1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Catabasis Pharmaceuticals2
PTC Therapeutics2
Scholar Rock, Inc.2
Avidity Biosciences, Inc.1
Baxalta now part of Shire1
Biohaven Pharmaceuticals, Inc.1
Fulcrum Therapeutics1
Kyntra Bio1
University of Rochester1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Neuromuscular Diseases12
Muscular Dystrophies8
Muscular Dystrophy, Duchenne7
Musculoskeletal Diseases7
Nervous System Diseases5
Genetic Diseases, Inborn4
Muscular Diseases4
Muscular Disorders, Atrophic4
Genetic Diseases, X-Linked3
Muscular Atrophy, Spinal3

Trials

Showing 1 to 12 of 12. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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