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Clinical trials

Neuromuscular Diseases trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Neuromuscular Diseases Country / region: United States Clear all

118 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20001
20013
20021
20031
20051
20061
20082
20094
20103
20114
20121
20136
20145
20156
20165
20176
20185
20197
20205
20219
20227
20234
20249
202510
20269

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed61
Recruiting25
Terminated15
Active, not recruiting8
Not yet recruiting3
Unknown status3
Available1
Withdrawn1
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
National Institute of Neurological Disorders and Stroke (NINDS)10
Columbia University9
Catabasis Pharmaceuticals3
Fulcrum Therapeutics3
National Institute of Nursing Research (NINR)3
PTC Therapeutics3
Scholar Rock, Inc.3
University of Pennsylvania3
Amylyx Pharmaceuticals Inc.2
Avidity Biosciences, Inc.2

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Neuromuscular Diseases118
Nervous System Diseases30
Muscular Dystrophies26
Musculoskeletal Diseases25
Muscular Diseases24
Muscular Dystrophy, Duchenne20
Amyotrophic Lateral Sclerosis18
Genetic Diseases, Inborn16
Muscular Atrophy, Spinal16
Neurodegenerative Diseases14

Trials

Showing 1 to 25 of 118. Each trial links to its page on Pharma Observatory.

18 more trials match. See them on Pharma Observatory

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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