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Clinical trials

Phase 1 Neuromuscular Diseases trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Neuromuscular Diseases Phase: Phase 1 Country / region: United States Clear all

6 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20181
20221
20232
20251
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed4
Not yet recruiting1
Recruiting1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Adjuvia Therapeutics, Inc.1
AstraZeneca1
Cabaletta Bio1
Edgewise Therapeutics, Inc.1
Johns Hopkins University1
PepGen Inc1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Neuromuscular Diseases6
Musculoskeletal Diseases5
Muscular Diseases4
Nervous System Diseases4
Genetic Diseases, Inborn3
Muscular Disorders, Atrophic2
Muscular Dystrophies2
Myositis2
Arthritis1
Arthritis, Rheumatoid1

Trials

Showing 1 to 6 of 6. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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