Clinical trials
Phase 1/2 Neuromuscular Diseases trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
10 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2008 | 1 |
| 2013 | 1 |
| 2014 | 1 |
| 2015 | 1 |
| 2016 | 1 |
| 2020 | 1 |
| 2021 | 1 |
| 2024 | 1 |
| 2025 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 5 |
| Active, not recruiting | 2 |
| Recruiting | 2 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Amylyx Pharmaceuticals Inc. | 1 |
| AskBio Inc | 1 |
| Catabasis Pharmaceuticals | 1 |
| Craig McDonald, MD | 1 |
| Ionis Pharmaceuticals, Inc. | 1 |
| National Institute of Nursing Research (NINR) | 1 |
| Thomas Advanced Medical LLC | 1 |
| University of Michigan | 1 |
| Vanda Pharmaceuticals | 1 |
| Vertex Pharmaceuticals Incorporated | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Neuromuscular Diseases | 10 |
| Nervous System Diseases | 4 |
| Musculoskeletal Diseases | 3 |
| Neurodegenerative Diseases | 3 |
| Amyotrophic Lateral Sclerosis | 2 |
| Muscular Diseases | 2 |
| Muscular Dystrophies | 2 |
| Muscular Dystrophy, Duchenne | 2 |
| Myotonic Dystrophy | 2 |
| Alzheimer Disease | 1 |
Trials
Showing 1 to 10 of 10. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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