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Clinical trials

Phase 2 Neuromuscular Diseases trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Neuromuscular Diseases Phase: Phase 2 Country / region: United States Clear all

14 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20131
20162
20173
20181
20192
20201
20221
20252
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed8
Terminated3
Active, not recruiting1
Enrolling by invitation1
Recruiting1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Flex Pharma, Inc.2
Fulcrum Therapeutics2
Amylyx Pharmaceuticals Inc.1
Avidity Biosciences, Inc.1
Capricor Inc.1
Craig McDonald, MD1
Emory University1
Neuraltus Pharmaceuticals, Inc.1
Satellos Bioscience, Inc.1
Scholar Rock, Inc.1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Neuromuscular Diseases14
Nervous System Diseases7
Muscular Dystrophies6
Neurodegenerative Diseases6
Amyotrophic Lateral Sclerosis5
Musculoskeletal Diseases4
Genetic Diseases, Inborn3
Motor Neuron Disease3
Muscular Diseases3
Muscular Disorders, Atrophic3

Trials

Showing 1 to 14 of 14. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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