Clinical trials
Sandhoff Disease trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
18 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2004 | 1 |
| 2006 | 1 |
| 2008 | 2 |
| 2010 | 2 |
| 2011 | 1 |
| 2012 | 2 |
| 2014 | 1 |
| 2015 | 1 |
| 2019 | 2 |
| 2020 | 1 |
| 2021 | 1 |
| 2022 | 1 |
| 2024 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 8 |
| Terminated | 5 |
| Recruiting | 3 |
| Active, not recruiting | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Masonic Cancer Center, University of Minnesota | 3 |
| University of Minnesota | 3 |
| Terence Flotte | 2 |
| Aldagen | 1 |
| Azafaros B.V. | 1 |
| Children's National Research Institute | 1 |
| Exsar Corporation | 1 |
| Genzyme, a Sanofi Company | 1 |
| Idorsia Pharmaceuticals Ltd. | 1 |
| IntraBio Inc | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Sandhoff Disease | 18 |
| Tay-Sachs Disease | 17 |
| Gangliosidoses, GM2 | 10 |
| Gangliosidosis, GM1 | 8 |
| Leukodystrophy, Globoid Cell | 7 |
| Adrenoleukodystrophy | 6 |
| Leukodystrophy, Metachromatic | 6 |
| Lysosomal Storage Diseases | 5 |
| Mucopolysaccharidosis III | 5 |
| alpha-Mannosidosis | 4 |
Trials
Showing 1 to 18 of 18. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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