Clinical trials
Observational Sandhoff Disease trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
6 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2010 | 2 |
| 2012 | 1 |
| 2019 | 1 |
| 2022 | 1 |
| 2024 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 3 |
| Recruiting | 2 |
| Active, not recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| University of Minnesota | 2 |
| Azafaros B.V. | 1 |
| Idorsia Pharmaceuticals Ltd. | 1 |
| Terence Flotte | 1 |
| University of Pittsburgh | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Sandhoff Disease | 6 |
| Tay-Sachs Disease | 6 |
| Gangliosidoses, GM2 | 5 |
| Gangliosidosis, GM1 | 3 |
| Gangliosidoses | 2 |
| Gaucher Disease | 2 |
| Lysosomal Storage Diseases | 2 |
| Genetic Diseases, Inborn | 1 |
| Leukodystrophy, Globoid Cell | 1 |
| Leukoencephalopathies | 1 |
Trials
Showing 1 to 6 of 6. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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