Clinical trials
Phase 1 Sandhoff Disease trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
3 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2008 | 1 |
| 2014 | 1 |
| 2021 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 1 |
| Terminated | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Exsar Corporation | 1 |
| Joanne Kurtzberg, MD | 1 |
| Terence Flotte | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Sandhoff Disease | 3 |
| Tay-Sachs Disease | 3 |
| Gangliosidoses, GM2 | 2 |
| Adrenoleukodystrophy | 1 |
| Brain Diseases, Metabolic, Inborn | 1 |
| Leukodystrophy, Globoid Cell | 1 |
| Leukodystrophy, Metachromatic | 1 |
| Lysosomal Storage Diseases | 1 |
| Mucopolysaccharidosis II | 1 |
| Neuronal Ceroid-Lipofuscinoses | 1 |
Trials
Showing 1 to 3 of 3. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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