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Clinical trials

Thalassemia trials in the United Kingdom

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Thalassemia Country / region: United Kingdom Clear all

19 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20031
20052
20072
20081
20091
20101
20142
20182
20192
20211
20222
20231
20251

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed13
Active, not recruiting2
Enrolling by invitation2
Recruiting1
Terminated1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Novartis Pharmaceuticals5
Vertex Pharmaceuticals Incorporated3
Agios Pharmaceuticals, Inc.2
Carelon Research2
UCSF Benioff Children's Hospital Oakland2
Bellicum Pharmaceuticals1
Celgene1
Forma Therapeutics, Inc.1
Nova Laboratories Limited1
Novo Nordisk A/S1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Thalassemia19
Anemia, Sickle Cell9
Anemia, Diamond-Blackfan6
Hemoglobinopathies6
beta-Thalassemia6
Anemia4
Genetic Diseases, Inborn4
Hematologic Diseases4
Myelodysplastic Syndromes4
Iron Overload3

Trials

Showing 1 to 19 of 19. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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