Clinical trials
Thalassemia trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
97 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 4 |
| 2001 | 1 |
| 2002 | 2 |
| 2003 | 3 |
| 2004 | 5 |
| 2005 | 2 |
| 2006 | 4 |
| 2007 | 2 |
| 2008 | 8 |
| 2009 | 8 |
| 2010 | 4 |
| 2011 | 4 |
| 2012 | 6 |
| 2013 | 1 |
| 2014 | 5 |
| 2015 | 3 |
| 2016 | 2 |
| 2017 | 3 |
| 2018 | 6 |
| 2019 | 5 |
| 2020 | 1 |
| 2021 | 1 |
| 2022 | 5 |
| 2023 | 1 |
| 2024 | 3 |
| 2025 | 4 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 60 |
| Terminated | 15 |
| Recruiting | 7 |
| Active, not recruiting | 7 |
| Unknown status | 3 |
| Withdrawn | 2 |
| Enrolling by invitation | 1 |
| Available | 1 |
| Approved for marketing | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Carelon Research | 7 |
| National Heart, Lung, and Blood Institute (NHLBI) | 6 |
| UCSF Benioff Children's Hospital Oakland | 6 |
| University of California, San Francisco | 6 |
| Novartis Pharmaceuticals | 5 |
| Novo Nordisk A/S | 4 |
| St. Jude Children's Research Hospital | 4 |
| Vertex Pharmaceuticals Incorporated | 4 |
| Baylor College of Medicine | 3 |
| Children's Hospital of Philadelphia | 3 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Thalassemia | 97 |
| Anemia, Sickle Cell | 57 |
| beta-Thalassemia | 23 |
| Hemoglobinopathies | 22 |
| Anemia, Diamond-Blackfan | 15 |
| Iron Overload | 13 |
| Genetic Diseases, Inborn | 8 |
| Fanconi Anemia | 7 |
| Hematologic Diseases | 7 |
| Immunologic Deficiency Syndromes | 7 |
Trials
Showing 1 to 25 of 97. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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