Clinical trials
Phase 1 Thalassemia trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
14 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2006 | 1 |
| 2008 | 2 |
| 2011 | 1 |
| 2014 | 1 |
| 2015 | 2 |
| 2017 | 1 |
| 2019 | 1 |
| 2024 | 2 |
| 2025 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 9 |
| Terminated | 3 |
| Active, not recruiting | 1 |
| Recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Heart, Lung, and Blood Institute (NHLBI) | 3 |
| Novo Nordisk A/S | 3 |
| National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | 2 |
| Bellicum Pharmaceuticals | 1 |
| Catherine Bollard | 1 |
| City of Hope Medical Center | 1 |
| Duke University | 1 |
| Sideris Pharmaceuticals | 1 |
| University of California, San Francisco | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Thalassemia | 14 |
| Anemia, Sickle Cell | 6 |
| Hemoglobinopathies | 5 |
| Iron Overload | 3 |
| Anemia, Diamond-Blackfan | 2 |
| Severe Combined Immunodeficiency | 2 |
| beta-Thalassemia | 2 |
| Anemia | 1 |
| Congenital Bone Marrow Failure Syndromes | 1 |
| Dyskeratosis Congenita | 1 |
Trials
Showing 1 to 14 of 14. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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