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Clinical trials

Phase 2 Thalassemia trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Thalassemia Phase: Phase 2 Country / region: United States Clear all

30 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20003
20011
20032
20044
20071
20082
20093
20101
20143
20171
20182
20194
20221
20231

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed17
Terminated7
Active, not recruiting3
Recruiting1
Unknown status1
Withdrawn1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Novartis Pharmaceuticals3
Baylor College of Medicine2
Carelon Research2
Memorial Sloan Kettering Cancer Center2
Agios Pharmaceuticals, Inc.1
Celgene1
Columbia University1
Dana-Farber Cancer Institute1
DisperSol Technologies, LLC1
Elliott Vichinsky1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Thalassemia30
Anemia, Sickle Cell19
beta-Thalassemia9
Hemoglobinopathies6
Anemia, Diamond-Blackfan5
Graft vs Host Disease3
Iron Overload3
Anemia2
Anemia, Aplastic2
Genetic Diseases, Inborn2

Trials

Showing 1 to 25 of 30. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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