Clinical trials
Completed Lysosomal Storage Diseases trials in Brazil
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
9 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2004 | 1 |
| 2007 | 1 |
| 2008 | 1 |
| 2011 | 2 |
| 2014 | 1 |
| 2015 | 1 |
| 2020 | 1 |
| 2022 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 9 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Shire | 3 |
| BioMarin Pharmaceutical | 2 |
| Alexion Pharmaceuticals, Inc. | 1 |
| Azafaros B.V. | 1 |
| Ultragenyx Pharmaceutical Inc | 1 |
| University of Pennsylvania | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lysosomal Storage Diseases | 9 |
| Mucopolysaccharidosis II | 3 |
| Sudden Infant Death | 3 |
| Gangliosidosis, GM1 | 2 |
| Genetic Diseases, Inborn | 2 |
| Metabolic Diseases | 2 |
| Mucopolysaccharidosis IV | 2 |
| Cholesterol Ester Storage Disease | 1 |
| Gangliosidoses, GM2 | 1 |
| Infant, Newborn, Diseases | 1 |
Trials
Showing 1 to 9 of 9. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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