Clinical trials
Observational Lysosomal Storage Diseases trials in France
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
7 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2008 | 1 |
| 2011 | 1 |
| 2015 | 2 |
| 2021 | 1 |
| 2022 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 4 |
| Terminated | 2 |
| Recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Alexion Pharmaceuticals, Inc. | 1 |
| Azafaros B.V. | 1 |
| BioMarin Pharmaceutical | 1 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 1 |
| Shire | 1 |
| University Hospital, Rouen | 1 |
| ZevraDenmark | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lysosomal Storage Diseases | 7 |
| Genetic Diseases, Inborn | 2 |
| Nervous System Diseases | 2 |
| Brain Diseases | 1 |
| Brain Diseases, Metabolic, Inborn | 1 |
| Central Nervous System Diseases | 1 |
| Cholesterol Ester Storage Disease | 1 |
| Demyelinating Diseases | 1 |
| Gangliosidoses, GM2 | 1 |
| Gangliosidosis, GM1 | 1 |
Trials
Showing 1 to 7 of 7. Each trial links to its page on Pharma Observatory.
Recently changed trials
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