Clinical trials
Completed Lysosomal Storage Diseases trials in France
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
14 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2004 | 1 |
| 2011 | 5 |
| 2013 | 1 |
| 2014 | 2 |
| 2015 | 1 |
| 2016 | 1 |
| 2019 | 1 |
| 2022 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 14 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Alexion Pharmaceuticals, Inc. | 4 |
| Shire | 3 |
| BioMarin Pharmaceutical | 2 |
| ZevraDenmark | 2 |
| Azafaros B.V. | 1 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 1 |
| Spark Therapeutics, Inc. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lysosomal Storage Diseases | 14 |
| Cholesterol Ester Storage Disease | 4 |
| Wolman Disease | 4 |
| Mucopolysaccharidosis II | 3 |
| Mucopolysaccharidosis IV | 2 |
| Niemann-Pick Disease, Type C | 2 |
| Sudden Infant Death | 2 |
| Gangliosidoses, GM2 | 1 |
| Gangliosidosis, GM1 | 1 |
| Genetic Diseases, Inborn | 1 |
Trials
Showing 1 to 14 of 14. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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