Clinical trials
Lysosomal Storage Diseases trials in Japan
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
4 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2011 | 2 |
| 2013 | 1 |
| 2015 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 3 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| BioMarin Pharmaceutical | 2 |
| Alexion Pharmaceuticals, Inc. | 1 |
| Shire | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lysosomal Storage Diseases | 4 |
| Mucopolysaccharidosis IV | 2 |
| Brain Diseases | 1 |
| Brain Diseases, Metabolic, Inborn | 1 |
| Central Nervous System Diseases | 1 |
| Cholesterol Ester Storage Disease | 1 |
| Demyelinating Diseases | 1 |
| Genetic Diseases, Inborn | 1 |
| Hereditary Central Nervous System Demyelinating Diseases | 1 |
| Leukodystrophy, Metachromatic | 1 |
Trials
Showing 1 to 4 of 4. Each trial links to its page on Pharma Observatory.
Recently changed trials
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