Clinical trials
Lysosomal Storage Diseases trials in the United States with no applicable phase
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
7 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2009 | 1 |
| 2011 | 1 |
| 2012 | 3 |
| 2017 | 1 |
| 2019 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 5 |
| Unknown status | 2 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Brigham and Women's Hospital | 1 |
| Masonic Cancer Center, University of Minnesota | 1 |
| Massachusetts General Hospital | 1 |
| Patricia I. Dickson, M.D. | 1 |
| Spark Therapeutics, Inc. | 1 |
| University of California, San Diego | 1 |
| University of Florida | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Lysosomal Storage Diseases | 7 |
| Metabolic Diseases | 3 |
| Glycogen Storage Disease Type II | 2 |
| Wolman Disease | 2 |
| Adrenoleukodystrophy | 1 |
| Cholesterol Ester Storage Disease | 1 |
| Cognitive Dysfunction | 1 |
| Cystinosis | 1 |
| Gangliosidosis, GM1 | 1 |
| Gaucher Disease | 1 |
Trials
Showing 1 to 7 of 7. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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