Clinical trials
Phase 1 Mucopolysaccharidosis II trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
5 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2005 | 1 |
| 2008 | 1 |
| 2014 | 1 |
| 2015 | 1 |
| 2022 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 3 |
| Recruiting | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Joanne Kurtzberg, MD | 2 |
| ArmaGen, Inc | 1 |
| Duke University | 1 |
| Homology Medicines, Inc | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis II | 5 |
| Metabolism, Inborn Errors | 2 |
| Mucopolysaccharidosis I | 2 |
| Sudden Infant Death | 2 |
| Adrenoleukodystrophy | 1 |
| Anemia, Aplastic | 1 |
| Anemia, Diamond-Blackfan | 1 |
| Brain Diseases, Metabolic, Inborn | 1 |
| Hematologic Neoplasms | 1 |
| Hemoglobinopathies | 1 |
Trials
Showing 1 to 5 of 5. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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